The award-winning WIRED UK Podcast with James Temperton and the rest of the team. Listen every week for the an informed and entertaining rundown of latest technology, science, business and culture news. New episodes every Friday.
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Content provided by Osmosis from Elsevier. All podcast content including episodes, graphics, and podcast descriptions are uploaded and provided directly by Osmosis from Elsevier or their podcast platform partner. If you believe someone is using your copyrighted work without your permission, you can follow the process outlined here https://podcastplayer.com/legal.
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A Transformational Time for Rare Disorders is Coming: Dr. Jessica Duis, VP of Clinical Development at GondolaBio
Manage episode 510077733 series 2984079
Content provided by Osmosis from Elsevier. All podcast content including episodes, graphics, and podcast descriptions are uploaded and provided directly by Osmosis from Elsevier or their podcast platform partner. If you believe someone is using your copyrighted work without your permission, you can follow the process outlined here https://podcastplayer.com/legal.
“Probably the most exciting thing I've seen in gene therapy over the last ten years is we now have a lot of tools for selective delivery, which will hopefully make treatments more safe and a lot more successful,” says Dr. Jessica Duis, a geneticist and pediatrician focused on the management of individuals with complex, rare disorders. Dr. Duis, who has worked on several gene therapies that are now approved or progressing through the accelerated approval pathway, is currently VP of Clinical Development at GondolaBio, a clinical-stage biopharmaceutical company focused on developing therapeutics for genetic diseases.
As you’ll learn in this Year of the Zebra episode with host Lindsey Smith, Dr. Duis is encouraged by other recent advances in genetic technology as well, and thinks momentum will grow as breakthrough treatments emerge. “I think we're hopefully going to continue to see companies that are working in rare disease be more successful and really drive how regulators think about making decisions in terms of bringing treatments to patients. I think we’re at the tip of the iceberg in terms of the future of truly transformational therapies.” This wide ranging conversation also explores Dr. Duis’ team approach to patient care, her work on clinical endpoints, the importance of patient communities, and her book series, Rare Siblings Stories.
Mentioned in this episode:
Elsevier Healthcare Hub on Rare Diseases
If you like this podcast, please share it on your social channels. You can also subscribe to the series and check out all of our episodes at www.osmosis.org/podcast
550 episodes
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Manage episode 510077733 series 2984079
Content provided by Osmosis from Elsevier. All podcast content including episodes, graphics, and podcast descriptions are uploaded and provided directly by Osmosis from Elsevier or their podcast platform partner. If you believe someone is using your copyrighted work without your permission, you can follow the process outlined here https://podcastplayer.com/legal.
“Probably the most exciting thing I've seen in gene therapy over the last ten years is we now have a lot of tools for selective delivery, which will hopefully make treatments more safe and a lot more successful,” says Dr. Jessica Duis, a geneticist and pediatrician focused on the management of individuals with complex, rare disorders. Dr. Duis, who has worked on several gene therapies that are now approved or progressing through the accelerated approval pathway, is currently VP of Clinical Development at GondolaBio, a clinical-stage biopharmaceutical company focused on developing therapeutics for genetic diseases.
As you’ll learn in this Year of the Zebra episode with host Lindsey Smith, Dr. Duis is encouraged by other recent advances in genetic technology as well, and thinks momentum will grow as breakthrough treatments emerge. “I think we're hopefully going to continue to see companies that are working in rare disease be more successful and really drive how regulators think about making decisions in terms of bringing treatments to patients. I think we’re at the tip of the iceberg in terms of the future of truly transformational therapies.” This wide ranging conversation also explores Dr. Duis’ team approach to patient care, her work on clinical endpoints, the importance of patient communities, and her book series, Rare Siblings Stories.
Mentioned in this episode:
Elsevier Healthcare Hub on Rare Diseases
If you like this podcast, please share it on your social channels. You can also subscribe to the series and check out all of our episodes at www.osmosis.org/podcast
550 episodes
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Similar to Raise the Line
The award-winning WIRED UK Podcast with James Temperton and the rest of the team. Listen every week for the an informed and entertaining rundown of latest technology, science, business and culture news. New episodes every Friday.
…
continue reading
Join expert voices from Barbell Logic and others from the world of strength for resources to help you get strong for life. Get coaching options and more educational content at barbell-logic.com.
…
continue reading
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…
continue reading
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…
continue reading
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continue reading
Welcome to Almost 30—a supportive space to fuel your conscious evolution. Join us, best friends Krista Williams + Lindsey Simcik, for heart-centered, hilarious conversations and raw, impactful interviews with brilliant guests. We dive deep into everything from modern spirituality and health + wellness to self-development, dating, and relationships. With every episode, our mission is to empower you, expand what you think is possible, and make you laugh—a lot. We’re honest, open, and above all ...
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The American healthcare system is one of the most innovative in the world. But it’s also riddled with complex challenges, such as access to affordable medications, inefficiency and administrative burdens, and communication barriers between providers. There’s clearly a better way—and at Surescripts, we have a unique sightline into what that may be. In this series, host Melanie Marcus, Chief Marketing Officer of Surescripts, sits down with today’s most inspiring and innovative leaders in healt ...
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